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Gene therapy is the technique in which defective or non-functional
genes are replaced with targeted gene. Gene therapy has gained
significant attention over the past two decades as a potential method
for treating genetic disorders such as severe combined
immunodeficiency, cystic fibrosis and Parkinson’s disease. Viral and
on-viral vectors commonly...
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Delivery of small interfering RNA (siRNA) for silencing of aberrantly expressed genes is a promising therapy for treatment of various genetic disorders. Polymeric carriers have been used in the design of efficient delivery systems to generate nanoscale siRNA polyplexes. Despite the great amount of research pursued on siRNA therapeutics, the underly...